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Myotonic dystrophy mouse models PacBio DMPK GSK3␤ Myostatin Dystrophin Therapy Male Trinucleotide repeat expansion Motoneuron Brain Glucocorticoids Glial cells Oligodendrocyte Skeletal muscle Myelin Myotonic dystrophy type 1 Trinucleotide Repeat Expansion Central nervous system Centronuclear myopathy Mouse models Exercice Dynamin 2 Cardiac muscle Heart Cells Heart failure CTG repeat instability Cell model Intermediate filament Dystrophie Myotonique Transgenic mouse model Oligodendrocytes Quantitative microdialysis Transcriptomics Acetylcholinesterase knockout mouse Dilated cardiomyopathy Gene editing ARN Gene therapy Antisense oligonucleotides Duchenne muscular dystrophy Autophagy Astrocytes Aging BIOLOGIE MOLECULAIRE Acetylcholinesterase deficiency Mouse model RNA interference Myotonic Dystrophy type 1 Diaphragm AAV Fibrosis RNA biology Mice DMSXL mice Muscular dystrophy CRISPR/Cas9 Antisense oligonucleotide Glutamate MBNL Cytoskeleton Maximal force Myotonic Dystrophy Type 1 CTG repeat contractions Genotype phenotype correlation ACETYLCHOLINESTERASE Desmin Transgenic mouse Endurance training CTG repeats Humans PCR Long read sequencing Acute coronary syndrome Glucocorticoid-receptor CMS Cell penetrating peptide Cultured CONGENITAL MYATHENIC SYNDROME Brain dysfunction GABA KNOCKOUT MICE Alternative splicing RNA splicing Animals Myotonic Dystrophy Muscle Astrocyte Exercise Expression Cell culture model Dystrophie myotonique DM1 Thérapie génique Gene Therapy Hypoxia Myotonic dystrophy Neuron CRISPRi